研究单位:[1]Safety and Efficacy Study of rAAV2-ND4 Treatment of LHON,Huazhong University of Science and Technology[2]Department of Ophthalmology,Tongji Hospital,Tongji Medical College,Huazhong University of Science and Technology Wuhan,Hubei,China,430030
研究目的:
This study is meant to assess the safety and efficacy of rAAV2-ND4 treatment of Leber hereditary optic neuropathy with 11778 LHON mutation.